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Table 1 Antisense oligonucleotides used in this study

From: Dual exon skipping in myostatin and dystrophin for Duchenne muscular dystrophy

AON

Targeting

Sequences (5'-3')

AON1

Myostatin exon 2

guuugaugagucucaggauu

AON2

Myostatin exon 2

gccaaauaccagugccu

AON3

Myostatin exon 2

agccaauuuugcaacacugu

h8AON3

Human dystrophin exon 8

guacauuaagauggacuuc

h44AON1

Human dystrophin exon 44

cgccgccauuucucaacag

h51AON1

Human dystrophin exon 51

ucaaggaagauggcauuucu

h54AON1

Human dystrophin exon 54

uacauuugucugccacugg

M23D (+02-18)

Mouse dystrophin exon 23

ggccaaaccucggcuuaccu