From: Dual exon skipping in myostatin and dystrophin for Duchenne muscular dystrophy
AON | Targeting | Sequences (5'-3') |
---|---|---|
AON1 | Myostatin exon 2 | guuugaugagucucaggauu |
AON2 | Myostatin exon 2 | gccaaauaccagugccu |
AON3 | Myostatin exon 2 | agccaauuuugcaacacugu |
h8AON3 | Human dystrophin exon 8 | guacauuaagauggacuuc |
h44AON1 | Human dystrophin exon 44 | cgccgccauuucucaacag |
h51AON1 | Human dystrophin exon 51 | ucaaggaagauggcauuucu |
h54AON1 | Human dystrophin exon 54 | uacauuugucugccacugg |
M23D (+02-18) | Mouse dystrophin exon 23 | ggccaaaccucggcuuaccu |